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◆ Journal of Market Access & Health Policy2026-08-04· Multiplicity (mathematics)

Guidance on Multiplicity Analysis in Single-Trial Assessments: A No-Solution Equation

Mondher Toumi, Bruno Fallissard, Asma Jouini, Pascal Auquier, Claude Dussart, Laurent Boyer

原始摘要(英文原文)· Original abstract
The European Health Technology Assessment (EU HTA) guidance on Multiplicity of Hypothesis Testing (MHT) [1] resembles an algebra no-solution equation. The hypothetico-deductive method used in inferential statistics, which this guidance references, relies on conclusive reasoning. However, the guidance fails to provide a clear resolution, leaving the matter to individual Member States (MS) despite its critical impact on statistical precision, a key pillar of validity in clinical trials for comparative effectiveness assessments in Joint Clinical Assessments (JCAs)
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