◆ European Respiratory Journal2025-11-27· Medicine
Advances in cystic fibrosis: CFTR modulator triple combinations
Pierre‐Régis Burgel, Marcus Mall
原始摘要(英文原文)· Original abstract
Shareable abstract Triple combinations of CFTR modulators have revolutionized the care of people with cystic fibrosis (CF). Initially developed for the F508del variant, these drugs are effective in many other CFTR variants, making them suitable for most, but not all, pwCF.