Marco Becilli, Pietro Merli, Mattia Algeri, Francesca Del Bufalo, Daria Pagliara, Valentina Bertaina, Chiara Agrati, Chiara Rosignoli, Maria Giuseppina Cefalo, Emilia Boccieri, Stefano Di Cecca, Laura Iaffaldano, Yunqin Lee, Biagio De Angelis, Soheil Meshinchi, Concetta Quintarelli, Dario Campana, Franco Locatelli
ABSTRACT: Autologous second-generation CD7-directed chimeric antigen receptor T cells, expressing an anti-CD7 protein expression blocker to prevent self-killing fratricide, were infused in 3 pediatric/young adult patients with relapsed/refractory CD7+ acute myeloid leukemia, resulting in measurable residual disease negativity. The safety profile was favorable.