Canping Chen, Yi Zhang, Xi Li, Tugba Y Ozmen, Furkan Ozmen, Shamilene Sivagnanam, Kyle P Gribbin, Katie E Blise, Xinxing Yang, Gangmin Kim, Roselyn S Dai, Dove Keith, Mara H Sherman, Mu-Shui Dai, Lisa M Coussens, Charles D Lopez, Rosalie C Sears, Gordon B Mills, Katelyn T Byrne, Zheng Xia
Pancreatic ductal adenocarcinoma (PDAC) is characterized by an immunosuppressive tumor microenvironment (TME) and poor prognosis. Although major histocompatibility complex class II (MHC-II) is typically expressed by professional antigen-presenting cells, its regulation and significance in malignant PDAC cells remain unclear. Here, we integrated single-cell RNA sequencing, spatial transcriptomics, bulk transcriptomics, multiplex immunohistochemistry, and functional studies in murine PDAC models to investigate tumor-cell MHC-II. Across human PDAC datasets, elevated tumor-cell MHC-II expression was associated with increased CD4⁺ and CD8⁺ T-cell infiltration and localization within immune-rich tumor niches. In paired biopsies from patients treated with cobimetinib, malignant cells showed increased expression of MHC-II pathway genes, suggesting therapy-induced activation of this program. In preclinical KPC models, MHC-IIhigh tumors exhibited greater T-cell infiltration, whereas MHC-IIlow tumors derived the greatest benefit from cobimetinib combined with immune checkpoint blockade. Mechanistically, direct tumor stimulation via in vitro administration of cobimetinib and recombinant interferon (IFN)-γ resulted in MHC-II induction in vitro by both MHCIIhigh and MHC-IIlow PDAC cell lines. In vivo, combined MEK inhibition and immune checkpoint blockade-controlled tumor growth, including in MHC-IIlow tumors. Deletion of the IFN-γ receptor abolished MHC-II induction and therapeutic benefit, demonstrating that this response is IFN-γ dependent. MEK inhibition enhanced downstream IFN-γ signaling and the combination was required for MHC II upregulation in vitro, indicating that MAPK activity restrains an IFN-γ-responsive MHC-II program. Collectively, these findings identify tumor-cell MHC-II as an IFN-γ-dependent, MAPK-restrained program that denotes immunotherapy sensitivity in PDAC.