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◆ Stem cell research2026-08-13

Derivation of a new induced pluripotent stem cell line ORIONi004-A for modelling Duchenne muscular dystrophy.

Dominika Hajduchova, Stanislava Suroviakova, Sandra Mersakova, Vladimir Nosal, Dusan Brany, Martin Rehak, Adela Blahova, Jakub Chmelar, Olga Chodelkova, Katarina Leskova Majdova, Henrieta Skovierova, Veronika Kucharikova, Slavomira Novakova, Zuzana Hatokova, Bibiana Badurova, Juraj Marcinek, Martin Jozef Pec, Robert Petrovic, Maria Fisherova, Miriama Juhosova, Barbora Mitruskova, Michal Pokusa, Andrea Evinova, Marek Samec, Matej Samos, Andreas Nicodemou, Lubos Danisovic, Dusan Dobrota, Egon Kurca, Katarina Lexova Kolejakova, Jan Chandoga, Lukas Plank, Martin Pec, Renata Pecova, Erika Halasova, Michal Kalman, Jan Strnadel

原始摘要(原文)
Anew in vitromodel for modeling Duchenne muscular dystrophy, derived from pediatric patient with a unique mutation in DMD gene is introduced. Peripheral blood was used as asource for primary cells (mononuclear cells) and subsequently reprogrammed into induced pluripotent stem cells with synthetic Sendai vector. Reprogrammed iPS cells showed the expression of pluripotency factors and the ability to differentiateinto all three germ layers.
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Derivation of a new induced pluripotent stem cell line ORIONi004-A for modelling Duchenne muscular dystrophy. — 科研速览 Science Skim